Paediatric Conditions
Rare diseases set the agenda for paediatric drug development
Many rare conditions begin in childhood, so orphan drug incentives and paediatric rules increasingly pull in the same direction.
Paediatric Conditions.
Developments across the diseases and disorders that affect children.
6 articlesUpdated 14 October 2026
More in Paediatric Conditions. Newest first.
Conditions
Why childhood cancers get so few new drugs, and the law trying to fix it
Childhood cancers are biologically distinct from adult ones, and for years that let new cancer drugs bypass children entirely. The RACE for Children Act changed the rules.
Conditions
The new era of RSV prevention for infants
For decades, protection against respiratory syncytial virus was reserved for the highest-risk babies. Long-acting antibodies and maternal vaccines have changed that.
Conditions
Type 1 diabetes in children: from closed loops to delaying the disease
Automated insulin delivery has transformed daily management. The bigger shift may be the first drug that delays type 1 diabetes before it starts.
Conditions
GLP-1 drugs for adolescents with obesity
The drugs reshaping adult obesity care are approved for teenagers too. Their arrival has forced a rethink of how childhood obesity is treated, and raised questions trials cannot yet answer.
Conditions
Duchenne muscular dystrophy and the accelerated approval debate
No paediatric disease has tested the FDA’s accelerated approval pathway like Duchenne. The arguments over dystrophin, function and risk are far from settled.
